TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease
Por um escritor misterioso
Descrição
Children with Niemann-Pick Type C (NPC), their parents and scientists seeking a treatment for this fatal genetic disease. WSJ follows this 6-year fight.
The complexity of a monogenic neurodegenerative disease: More than two decades of therapeutic driven research into Niemann-Pick type C disease - ScienceDirect
Push to spur drugs for deadly rare diseases
What is Niemann-Pick Type C Disease?
Niemann-Pick Disease Type C
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Niemann–Pick Disease Type C
Niemann-Pick Type C Disease - NP-C Genetic Disease - Lysosomal Disease
Your Impact - Ara Parseghian Medical Research Fund
Families plead with FDA for drug to treat Niemann-Pick Disease Type C
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por adulto (o preço varia de acordo com o tamanho do grupo)
